Gene therapy partnering routes (Rocket, Forge, Andelyn, AskBio)
Various gene therapy companies
No company currently runs an open application program in this space. Rocket Pharmaceuticals has three clinical-stage inherited-cardiomyopathy AAV programs (PKP2-ACM, Danon, BAG3-DCM) and has originated programs from academic labs. Forge Biologics has subsidised manufacturing for patient-foundation programs, including the Progeria Research Foundation, and sits in the NIH Bespoke Gene Therapy Consortium. Andelyn Biosciences and AskBio are academic-adjacent AAV manufacturers.
BSF documents the AAV-TAZ preclinical science base, but no industry partner has been publicly named. These are the companies whose existing cardiomyopathy or foundation-partnership track record makes them the plausible approach.
Academic labs and foundations with gene-therapy programs seeking an industry partner or manufacturing.
Engagement runs through business-development outreach and cardiology/gene-therapy congresses rather than portals.
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Last updated August 28, 2026 · Suggest an update to this entry